| ★ | Mission Moment: Janelle finds new hope through groundbreaking gene therapy | Children's Health @childrens | 1.2K | Estados Unidos | |
| 4 | CHLA's First Commercial Dose of Hemgenix (Gene Therapy) | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | — | Estados Unidos | 87 |
| 18 | Once Upon a Clementine | St. Louis Children's Hospital @childrenshospitalstl | — | Estados Unidos | 85 |
| 9 | Children's Health | Turning Hopes Into Reality | Children's Health @childrens | 107.5K | Estados Unidos | 86 |
| 11 | Baby KJ One Year Later: Gene-Editing Breakthrough Update | The Children's Hospital of Philadelphia @childrenshospphila | 12.0K | Estados Unidos | 85 |
| 1 | Day in the Life: Gene Therapy for Sickle Cell Disease | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.8K | Estados Unidos | 88 |
| 10 | He was the first person in the world to try this gene therapy | | 2.5K | Reino Unido | 86 |
| 16 | Janelle Monáe Visits Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.4K | Estados Unidos | 85 |
| 12 | Nicholas’s Journey: Gene Therapy Offers Hope for Leukodystrophy | The Children's Hospital of Philadelphia @childrenshospphila | 2.3K | Estados Unidos | 85 |
| 8 | First gene therapy to treat hereditary hearing loss approved by the FDA! | Boston Children's Hospital @childrenshospital | 2.0K | Estados Unidos | 86 |
| 19 | Ryan's Miraculous Hemophilia B Recovery with Hemgenix Gene Therapy | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 1.2K | Estados Unidos | 85 |
| 20 | Why Genetic Diagnoses Take So Long for Kids | CareTalk: Healthcare. Unfiltered. Podcast @caretalkpodcast | 1.1K | Estados Unidos | 85 |
| 2 | Gene Therapy at CHLA Revolutionizes Hemophilia Treatment | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 953 | Estados Unidos | 88 |
| 13 | Curing Childhood Cancer with Dr. James Amatruda: Expert Insights | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 623 | Estados Unidos | 85 |
| 3 | Gene Therapy Gave Ashlyn Her Sight Back | A CHLA Breakthrough Story | Children's Hospital Los Angeles @childrensla | 342 | Estados Unidos | 87 |
| 6 | Mission Moment: Children's Health patient KK meets the donor who changed her future | Children's Health @childrens | 306 | Estados Unidos | 86 |
| 17 | Avery's Incredible Moments | Children's Health @childrens | 208 | Estados Unidos | 85 |
| 7 | How Skysona Gene Therapy Is Changing Care for Boys with ALD | Children's Health @childrens | 141 | Estados Unidos | 86 |
| 14 | Preparing Families for the Exa-cel Gene Therapy Journey, With Haydar Frangoul, MD, MS | | 109 | Estados Unidos | 85 |
| 5 | After Sickle Cell Gene Therapy, What Comes Next? | | 78 | Estados Unidos | 86 |
| 15 | Richard shares his daughter’s remarkable journey with gene therapy. | | 76 | Estados Unidos | 85 |