| ★ | Nicholas’s Journey: Gene Therapy Offers Hope for Leukodystrophy | The Children's Hospital of Philadelphia @childrenshospphila | 2.3K | Estados Unidos | |
| 10 | Family Fights for Gene Therapy to Save Their Son | Your Morning | CTV Your Morning @ctvyourmorning | — | Canadá | 86 |
| 1 | Baby KJ One Year Later: Gene-Editing Breakthrough Update | The Children's Hospital of Philadelphia @childrenshospphila | 12.0K | Estados Unidos | 87 |
| 11 | What If We Can Get To Them Before They Have Symptoms?: How Florida Passed The Sunshine Genetics Law | CNBC Television @cnbctelevision | 6.7K | Estados Unidos | 86 |
| 5 | Day in the Life: Gene Therapy for Sickle Cell Disease | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.8K | Estados Unidos | 87 |
| 2 | Living with Spina Bifida: Harper’s Journey from Diagnosis to Hope | The Children's Hospital of Philadelphia @childrenshospphila | 1.3K | Estados Unidos | 87 |
| 20 | Mission Moment: Janelle finds new hope through groundbreaking gene therapy | Children's Health @childrens | 1.2K | Estados Unidos | 85 |
| 4 | Gene Therapy Turns Rare Disease Research into Care | University of California Television (UCTV) @uctv | 961 | Estados Unidos | 87 |
| 6 | Gene Therapy at CHLA Revolutionizes Hemophilia Treatment | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 953 | Estados Unidos | 86 |
| 7 | Curing Childhood Cancer with Dr. James Amatruda: Expert Insights | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 623 | Estados Unidos | 86 |
| 14 | First gene therapy in a baby with OTC deficiency, a rare urea cycle disorder | Hospital Sant Joan de Déu Barcelona @sjdhospitalbarcelona | 622 | España | 86 |
| 9 | COMPASS TO MS CARE-Updates and New Treatments | The MS Views and News Learning Channel @msviewsandnews | 457 | Estados Unidos | 86 |
| 3 | Gene Therapy Gave Ashlyn Her Sight Back | A CHLA Breakthrough Story | Children's Hospital Los Angeles @childrensla | 342 | Estados Unidos | 87 |
| 17 | MS COMPASS TO CARE-Benefits and Risks of MS treatment options, research updates | The MS Views and News Learning Channel @msviewsandnews | 268 | Estados Unidos | 86 |
| 16 | MS, NMOSD, and MOG medications and optic issues, racial and ethnic disparities | The MS Views and News Learning Channel @msviewsandnews | 155 | Estados Unidos | 86 |
| 18 | How Skysona Gene Therapy Is Changing Care for Boys with ALD | Children's Health @childrens | 141 | Estados Unidos | 86 |
| 8 | Leveraging Innovative Trial Designs and Technologies to Accelerate - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 129 | Estados Unidos | 86 |
| 15 | Richard shares his daughter’s remarkable journey with gene therapy. | | 76 | Estados Unidos | 86 |
| 12 | Does Autism Have a Cure? What Science Really Says | Mental Health Institute of Florida @mentalhealthinstituteofflorida | 49 | Estados Unidos | 86 |
| 19 | Camara: Love in Action - Mexico 1 | Camara Cassin @themaraglow | 16 | — | 85 |
| 13 | Study: Video Game May Help More With Duchenne | MediaSourceTV @mediasourcetv | 5 | — | 86 |