| ★ | Gene Therapy Gave Ashlyn Her Sight Back | A CHLA Breakthrough Story | Children's Hospital Los Angeles @childrensla | 342 | Estados Unidos | |
| 4 | CHLA's First Commercial Dose of Hemgenix (Gene Therapy) | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | — | Estados Unidos | 88 |
| 20 | MrBeast Visits Patients | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 30.1K | Estados Unidos | 86 |
| 13 | Celebrating 125 Years of Hope and Healthier Futures | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 4.0K | Estados Unidos | 86 |
| 2 | Day in the Life: Gene Therapy for Sickle Cell Disease | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.8K | Estados Unidos | 89 |
| 9 | Abigail Learns to Walk! | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.8K | Estados Unidos | 87 |
| 14 | Goodbye, 2025! | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.5K | Estados Unidos | 86 |
| 6 | Nicholas’s Journey: Gene Therapy Offers Hope for Leukodystrophy | The Children's Hospital of Philadelphia @childrenshospphila | 2.3K | Estados Unidos | 87 |
| 8 | Toddler Puts on Glasses for the First Time! | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.0K | Estados Unidos | 87 |
| 16 | Epilepsy Surgery Changed His Life | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.0K | Estados Unidos | 86 |
| 10 | Sofia Goes Home with New Liver | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.0K | Estados Unidos | 87 |
| 18 | #177 - Can Stem Cell Therapy Help Autism? Here's What the Science Says | | 1.7K | Estados Unidos | 86 |
| 5 | Mission Moment: Janelle finds new hope through groundbreaking gene therapy | Children's Health @childrens | 1.2K | Estados Unidos | 88 |
| 11 | Alyson Rings the Bell! | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 1.2K | Estados Unidos | 86 |
| 17 | Ryan's Miraculous Hemophilia B Recovery with Hemgenix Gene Therapy | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 1.2K | Estados Unidos | 86 |
| 15 | Stem Cells Restore Vision? AMD Breakthrough! | | 957 | Estados Unidos | 86 |
| 1 | Gene Therapy at CHLA Revolutionizes Hemophilia Treatment | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 953 | Estados Unidos | 89 |
| 3 | Curing Childhood Cancer with Dr. James Amatruda: Expert Insights | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 623 | Estados Unidos | 88 |
| 12 | Goodbye, 2024! | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 190 | Estados Unidos | 86 |
| 19 | Preparing Families for the Exa-cel Gene Therapy Journey, With Haydar Frangoul, MD, MS | | 109 | Estados Unidos | 86 |
| 7 | Richard shares his daughter’s remarkable journey with gene therapy. | | 76 | Estados Unidos | 87 |