| ★ | Preparing Families for the Exa-cel Gene Therapy Journey, With Haydar Frangoul, MD, MS | | 109 | Estados Unidos | |
| 11 | CHLA's First Commercial Dose of Hemgenix (Gene Therapy) | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | — | Estados Unidos | 85 |
| 15 | China Launches First CAR-T Therapy for Solid Tumours | | 1.6M | Reino Unido | 84 |
| 16 | Baby KJ One Year Later: Gene-Editing Breakthrough Update | The Children's Hospital of Philadelphia @childrenshospphila | 12.0K | Estados Unidos | 84 |
| 6 | Day in the Life: Gene Therapy for Sickle Cell Disease | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 2.8K | Estados Unidos | 85 |
| 5 | Nicholas’s Journey: Gene Therapy Offers Hope for Leukodystrophy | The Children's Hospital of Philadelphia @childrenshospphila | 2.3K | Estados Unidos | 85 |
| 2 | First gene therapy to treat hereditary hearing loss approved by the FDA! | Boston Children's Hospital @childrenshospital | 2.0K | Estados Unidos | 85 |
| 9 | #177 - Can Stem Cell Therapy Help Autism? Here's What the Science Says | | 1.7K | Estados Unidos | 85 |
| 4 | Mission Moment: Janelle finds new hope through groundbreaking gene therapy | Children's Health @childrens | 1.2K | Estados Unidos | 85 |
| 19 | Gene Therapy Turns Rare Disease Research into Care | University of California Television (UCTV) @uctv | 961 | Estados Unidos | 84 |
| 3 | Gene Therapy at CHLA Revolutionizes Hemophilia Treatment | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 953 | Estados Unidos | 85 |
| 13 | Curing Childhood Cancer with Dr. James Amatruda: Expert Insights | Children's Hospital Los Angeles | Children's Hospital Los Angeles @childrensla | 623 | Estados Unidos | 84 |
| 8 | First gene therapy in a baby with OTC deficiency, a rare urea cycle disorder | Hospital Sant Joan de Déu Barcelona @sjdhospitalbarcelona | 622 | España | 85 |
| 7 | Gene Therapy Gave Ashlyn Her Sight Back | A CHLA Breakthrough Story | Children's Hospital Los Angeles @childrensla | 342 | Estados Unidos | 85 |
| 20 | Provider Connections: Dr. Saad Kenderian on Updates in CAR-T Therapy in Chronic Lymphocytic Leukemia | | 228 | Estados Unidos | 84 |
| 17 | Functional Cures for T1D: Insulin Independence Through Islet Transplantation | | 185 | Estados Unidos | 84 |
| 18 | Le régime cétogène expliqué simplement | | 169 | Francia | 84 |
| 1 | Exa-Cel Approval Expands to Children as Young as 2 With Haydar Frangoul, MD | | 100 | Estados Unidos | 89 |
| 10 | After Sickle Cell Gene Therapy, What Comes Next? | | 78 | Estados Unidos | 85 |
| 14 | Richard shares his daughter’s remarkable journey with gene therapy. | | 76 | Estados Unidos | 84 |
| 12 | Diabetes Dialogue: Teplizumab, Stelo, and Inhaled Insulin Afrezza for Pediatric Patients | | 53 | Estados Unidos | 84 |