Similares a IAMRARE Testimonial: Coalition to Cure Calpain 3
20 vecinos (text_768) · 77 views · National Organization for Rare Disorders (NORD) · Estados Unidos
| ★ | IAMRARE Testimonial: Coalition to Cure Calpain 3 | National Organization for Rare Disorders (NORD) @raredisorders | 77 | Estados Unidos | |
| 18 | ERN ReCONNET video to launch the RARE DISEASES AWARENESS MONTH 2024! | ERN ReCONNET @ernreconnet | 360 | — | 83 |
| 13 | Understanding the FDA's Plausible Mechanism Framework | National Organization for Rare Disorders (NORD) @raredisorders | 276 | Estados Unidos | 84 |
| 12 | NORD® Rare Disease Scientific Symposium 2025 | National Organization for Rare Disorders (NORD) @raredisorders | 173 | Estados Unidos | 84 |
| 9 | From Voices to Breakthroughs: The 2025 NORD Breakthrough Summit | National Organization for Rare Disorders (NORD) @raredisorders | 159 | Estados Unidos | 85 |
| 14 | Stay Covered: Open Enrollment Essentials for Rare Disease Families | National Organization for Rare Disorders (NORD) @raredisorders | 152 | Estados Unidos | 84 |
| 7 | Leveraging Innovative Trial Designs and Technologies to Accelerate - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 129 | Estados Unidos | 86 |
| 20 | National Strategic Action Plan for Rare Diseases | Rare Voices Australia @rarevoicesaustralia2025 | 105 | Australia | 83 |
| 6 | Registries and Real World Data as Development Platforms - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 99 | Estados Unidos | 87 |
| 8 | Learn How to Support Our Rare Disease Citizen Petition to the FDA | National Organization for Rare Disorders (NORD) @raredisorders | 76 | Estados Unidos | 85 |
| 11 | What’s Next in Rare Disease Data Collection and Clinical Use - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 70 | Estados Unidos | 84 |
| 3 | IAMRARE Testimonial: 17q12 Foundation | National Organization for Rare Disorders (NORD) @raredisorders | 63 | Estados Unidos | 92 |
| 16 | NORD®'s 2025 Rare Disease Advisory Council Stakeholders Webinar | National Organization for Rare Disorders (NORD) @raredisorders | 61 | Estados Unidos | 84 |
| 1 | IAMRARE Testimonial: FamilieSCN2A Foundation | National Organization for Rare Disorders (NORD) @raredisorders | 56 | Estados Unidos | 93 |
| 2 | IAMRARE Testimonial: Association for Creatine Deficiencies | National Organization for Rare Disorders (NORD) @raredisorders | 56 | Estados Unidos | 93 |
| 19 | Voices of PLWRD and PLWUD from around the world in support of the #Resolution4Rare | Rare Diseases International @rarediseasesinternational3378 | 49 | — | 83 |
| 10 | Mobilize for Newborn Screening: Tools for Advocates During Awareness Month | National Organization for Rare Disorders (NORD) @raredisorders | 44 | Estados Unidos | 84 |
| 4 | IAMRARE Testimonial: Chondrosarcoma Foundation | National Organization for Rare Disorders (NORD) @raredisorders | 35 | Estados Unidos | 87 |
| 17 | #ACT4RARE Toolkit Launch - Webinar - 12.10.2022 | Rare Diseases International @rarediseasesinternational3378 | 25 | — | 84 |
| 5 | How to Volunteer to Spread Rare Disease Awareness with NORD | National Organization for Rare Disorders (NORD) @raredisorders | 23 | Estados Unidos | 87 |
| 15 | How To Build Effective Coalitions For MD Advocacy? - Muscular Dystrophy Support Network | Muscular Dystrophy Support Network @musculardystrophynetwork | 1 | Estados Unidos | 84 |




















