| ★ | Rare disease families find roadmap to drug development at bootcamps | CNBC Television @cnbctelevision | 2.4K | Estados Unidos | |
| 2 | The not-so-rare world of rare diseases | Zhenghong Gao | TEDxApex | | 529.9K | Estados Unidos | 85 |
| 5 | How Genomics Is Transforming Rare Disease Care w/ Katherine Stueland, CEO, GeneDX | CareTalk: Healthcare. Unfiltered. Podcast @caretalkpodcast | 8.4K | Estados Unidos | 85 |
| 18 | STEIN Fireside Podcast: Ep5-Shorts-4 | | 1.4K | Estados Unidos | 84 |
| 11 | 'Rare' diseases: 1 billion reasons to care | | 1.3K | Suiza | 84 |
| 9 | Gene Therapy Turns Rare Disease Research into Care | University of California Television (UCTV) @uctv | 961 | Estados Unidos | 84 |
| 17 | Newborns, Rare Diseases and Family Strength - Real Parenting Stories | Absolute Documentaries @absolutedocumentaries | 753 | Reino Unido | 84 |
| 4 | Rewriting the Rules: Scaling Innovation for Rare Diseases | Global Conference 2026 | Milken Institute @milkeninstitute | 497 | Estados Unidos | 85 |
| 20 | What Sequencing Healthy Newborns Revealed | CareTalk: Healthcare. Unfiltered. Podcast @caretalkpodcast | 477 | Estados Unidos | 84 |
| 15 | ERN ReCONNET video to launch the RARE DISEASES AWARENESS MONTH 2024! | | 360 | — | 84 |
| 6 | Understanding the FDA's Plausible Mechanism Framework | National Organization for Rare Disorders (NORD) @raredisorders | 276 | Estados Unidos | 85 |
| 1 | Leveraging Innovative Trial Designs and Technologies to Accelerate - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 129 | Estados Unidos | 86 |
| 3 | Registries and Real World Data as Development Platforms - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 99 | Estados Unidos | 85 |
| 16 | NORD Rare Disease Centers of Excellence Grand Rounds | Rare Disease Day 2026 | National Organization for Rare Disorders (NORD) @raredisorders | 79 | Estados Unidos | 84 |
| 12 | Improving rare disease diagnosis and prognosis with yeast functional assays | | 75 | Estados Unidos | 84 |
| 8 | UHC Day 2020 - Universal Health Coverage for Rare Diseases | Rare Diseases International @rarediseasesinternational3378 | 74 | — | 85 |
| 13 | Day Two at the Global Genes Rare Drug Development Symposium 2025 | | 46 | — | 84 |
| 14 | Raising Awareness of Rare Diseases | BoysTownHospital @boystownhospital | 41 | Estados Unidos | 84 |
| 19 | Raising Awareness for a Rare Neurological Disease | | 6 | Estados Unidos | 84 |
| 7 | Khure Health: Enabling the advancement of awareness and education on rare diseases. | Khure Health @khurehealth4579 | 1 | Canadá | 85 |
| 10 | Fair For Rare: Call for a National Rare Disease Framework | Rare Voices Australia @rarevoicesaustralia2025 | 1 | Australia | 84 |