| ★ | World-first gene therapy for a rare immune condition | Wellcome | | 1.1K | Reino Unido | |
| 6 | #167 - Stem Cell Therapy in Autoimmune Disease and Long COVID | | — | Estados Unidos | 85 |
| 9 | Family Fights for Gene Therapy to Save Their Son | Your Morning | CTV Your Morning @ctvyourmorning | — | Canadá | 85 |
| 14 | New Medical Treatment Saved This Little Boy’s Life | | — | — | 84 |
| 17 | Once Upon a Clementine | St. Louis Children's Hospital @childrenshospitalstl | — | Estados Unidos | 84 |
| 20 | #160 - Evidence Behind Stem Cell Therapy in Diverse Disease Conditions | | — | Estados Unidos | 84 |
| 13 | Scientists Cure 3 Diseases With Single Injection | | 9.4M | Reino Unido | 84 |
| 19 | How Genomics Is Transforming Rare Disease Care w/ Katherine Stueland, CEO, GeneDX | CareTalk: Healthcare. Unfiltered. Podcast @caretalkpodcast | 8.4K | Estados Unidos | 84 |
| 18 | How Rare Disease Patients Are Rewriting The Rules Of Medicine | | 8.0K | — | 84 |
| 1 | He was the first person in the world to try this gene therapy | | 2.5K | Reino Unido | 95 |
| 12 | Nicholas’s Journey: Gene Therapy Offers Hope for Leukodystrophy | The Children's Hospital of Philadelphia @childrenshospphila | 2.3K | Estados Unidos | 84 |
| 10 | First gene therapy to treat hereditary hearing loss approved by the FDA! | Boston Children's Hospital @childrenshospital | 2.0K | Estados Unidos | 85 |
| 11 | Mission Moment: Janelle finds new hope through groundbreaking gene therapy | Children's Health @childrens | 1.2K | Estados Unidos | 85 |
| 3 | Gene Therapy Turns Rare Disease Research into Care | University of California Television (UCTV) @uctv | 961 | Estados Unidos | 87 |
| 2 | Changing lives through science | Wellcome | | 735 | Reino Unido | 91 |
| 7 | First gene therapy in a baby with OTC deficiency, a rare urea cycle disorder | Hospital Sant Joan de Déu Barcelona @sjdhospitalbarcelona | 622 | España | 85 |
| 5 | IVF science breaking the cycle of inherited disease | Wellcome | | 501 | Reino Unido | 85 |
| 16 | Reversing Autoimmune Disease with Stem Cells | Brave New Us with Samantha N Stephenson @samanthanstephenson | 138 | Estados Unidos | 84 |
| 4 | Richard shares his daughter’s remarkable journey with gene therapy. | | 76 | Estados Unidos | 86 |
| 15 | How Gene Therapy Is Transforming Healthcare – The Future of Disease Treatment | 머니렙아크 MoneyRepArc @머니렙아크moneyreparc | 0 | Corea del Sur | 84 |