| ★ | mRNA Therapy Explained: The Future of Protein Replacement | National Organization for Rare Disorders (NORD) @raredisorders | 203 | Estados Unidos | |
| 4 | From Sick to Healed? How DNA Editing Is Changing the Game | | 11.4K | Estados Unidos | 86 |
| 20 | Gene Therapy Breakthrough: Silencing Brain Disease #shorts | Neuromuscular Medicine Expert @neuromuscularexpert | 1.6K | — | 84 |
| 3 | The Science Behind Gene Therapy Promise and Challenges (2 Minutes) | BioTech Whisperer @biotechwhisperer | 1.5K | Estados Unidos | 87 |
| 14 | She uses AI to design new cures for disease - Christina Theodoris - Young American Scientists 2026 | Scientific American @scientificamerican | 924 | Estados Unidos | 84 |
| 7 | There is No Reason We Cant Treat Diseases Now. | Berggruen Institute @berggrueninst | 770 | Estados Unidos | 86 |
| 12 | First gene therapy in a baby with OTC deficiency, a rare urea cycle disorder | Hospital Sant Joan de Déu Barcelona @sjdhospitalbarcelona | 622 | España | 85 |
| 18 | The Role of Bioinformatics in Drug Discovery | BioTech Whisperer @biotechwhisperer | 550 | Estados Unidos | 84 |
| 2 | Editing Genes to Cure Disease -- Gene Therapy explain in under 45s | | 416 | Vietnam | 87 |
| 1 | Understanding Enzyme Replacement Therapy | National Organization for Rare Disorders (NORD) @raredisorders | 290 | Estados Unidos | 88 |
| 13 | Understanding the FDA's Plausible Mechanism Framework | National Organization for Rare Disorders (NORD) @raredisorders | 276 | Estados Unidos | 84 |
| 11 | The genetic technology that could slow, stop, or reverse chronic disease [Ad Content from Alnylam] | | 141 | — | 85 |
| 17 | Leveraging Innovative Trial Designs and Technologies to Accelerate - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 129 | Estados Unidos | 84 |
| 19 | Perfection through Gene Editing | YouTube Shorts | #GeneEditing #GeneticPerfection #CRISPR #shorts | | 86 | India | 84 |
| 10 | Pompe Disease Breakthrough: Gene Therapy & Oral Drugs Revolutionize Treatment #shorts | Neuromuscular Medicine Expert @neuromuscularexpert | 81 | — | 85 |
| 15 | Immunopharmacology & Gene Therapy | Chapter 46 – Brenner & Stevens’ Pharmacology (6th) | Last Minute Lecture @lastminutelecture | 25 | Estados Unidos | 84 |
| 6 | How Scientists Are Rewriting Human DNA — Gene Therapy Explained🧬🧪 | | 10 | Vietnam | 86 |
| 8 | Nobel Prize 2023 Medicine The mRNA Revolution | | 6 | India | 85 |
| 5 | How Gene Therapy Is Transforming Healthcare – The Future of Disease Treatment | 머니렙아크 MoneyRepArc @머니렙아크moneyreparc | 0 | Corea del Sur | 86 |
| 9 | The future of gene therapy | Blue Current @bluecurrent7 | 0 | India | 85 |