| ★ | CORD Workshop - Knowledge Sharing on Advanced Therapies | Rare Diseases International @rarediseasesinternational3378 | 34 | — | |
| 4 | Session 2: Panel Discussion - Lifting barriers to novel therapies | Institut du Cerveau - Paris Brain Institute @institutducerveau | — | Francia | 85 |
| 12 | Cellular, Tissue and Gene Therapies Advisory Committee (CTGTAC) Meeting | U.S. Food and Drug Administration @us_fda | 27.0K | Estados Unidos | 84 |
| 10 | Where Innovation Meets Patients: The Work of California’s Alpha Clinics | University of California Television (UCTV) @uctv | 2.0K | Estados Unidos | 84 |
| 6 | Gene Therapy Turns Rare Disease Research into Care | University of California Television (UCTV) @uctv | 961 | Estados Unidos | 85 |
| 19 | Rewriting the Rules: Scaling Innovation for Rare Diseases | Global Conference 2026 | Milken Institute @milkeninstitute | 497 | Estados Unidos | 84 |
| 3 | Leveraging Innovative Trial Designs and Technologies to Accelerate - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 129 | Estados Unidos | 85 |
| 11 | Adaptive and platform trials | | 120 | Estados Unidos | 84 |
| 5 | Registries and Real World Data as Development Platforms - NORD Scientific Symposium | National Organization for Rare Disorders (NORD) @raredisorders | 99 | Estados Unidos | 85 |
| 15 | A Cell- and Circuit-level Approach to Understanding and Treating Brain Diseases | | 84 | Estados Unidos | 84 |
| 17 | Learn About Induced Pluripotent Stem Cells | BioTech Whisperer @biotechwhisperer | 74 | Estados Unidos | 84 |
| 7 | Session 2: Accelerating therapies & prevention - Matthias Tschöp | Institut du Cerveau - Paris Brain Institute @institutducerveau | 62 | Francia | 85 |
| 14 | Panel Discussion on the Value of Networked Care Globally | Rare Diseases International @rarediseasesinternational3378 | 60 | — | 84 |
| 13 | Unlocking the Future of Regenerative Medicine Challenges and Innovations 🧬 | Microlearning Daily @microlearningdaily | 38 | Singapur | 84 |
| 9 | Stem Cells and Regenerative Medicine (10 Minutes) | Technology Whisper @technologywhisper | 34 | Singapur | 84 |
| 18 | A Lecture and Panel Discussion to Honor the Life, Scholarship, and Impact of Carlton Haywood Jr, PhD | Berman Institute @bermaninstitute | 26 | — | 84 |
| 20 | Leading the way in Cell & Gene Therapy | | 24 | Irlanda | 84 |
| 1 | CORD Workshop 3 - Knowledge Sharing on Advanced Therapies | Rare Diseases International @rarediseasesinternational3378 | 12 | — | 91 |
| 2 | CORD Workshop 2 - Knowledge-Sharing on Advanced Therapies | Rare Diseases International @rarediseasesinternational3378 | 12 | — | 90 |
| 8 | Mini Symposium Cell Based Therapies | RCMI Program UPR Medical Sciences Campus @ciartech | 6 | — | 84 |
| 16 | Why Is Equitable Access Critical In Genetic Therapies? | Everyday Bioethics Expert @everydaybioethicsexpert | 1 | Estados Unidos | 84 |